Global Research & Clinical Trials in Charcot-Marie-Tooth (CMT) Disease
Stay informed about ongoing research and future treatment possibilities.
At the Charcot Marie Tooth Foundation of India,
we aim to keep the patient community informed about research and clinical developments in Charcot-Marie-Tooth (CMT) disease around the world.
To achieve this goal, we are committed to raising awareness and improving access to reliable CMT information. As part of this effort, this page provides a curated overview of international research initiatives, clinical trials, emerging therapies, scientific publications, and data-driven research.
In addition, the information comes from publicly available sources and trusted institutions. Therefore, our goal is to make important developments easier for the CMT community to understand and follow.
Furthermore, we cover research across several key areas. These include gene therapy, drug development, neuromuscular rehabilitation, AI-based modeling, and patient-focused research.
Through this platform, we aim to keep patients, families, caregivers, healthcare professionals, and researchers informed about the latest progress in CMT research and treatment. Ultimately, we hope to make reliable research updates more accessible to the entire CMT community.
Disclaimer:
We do not conduct, fund, or manage the research projects or clinical trials mentioned on this website. All studies are carried out by independent researchers, institutions, and organizations. Information is shared solely for awareness and educational purposes.
In addition to sharing global research updates, we are working to build a National CMT Patient Data Registry in India. The registry will help us better understand the needs, experiences, and disease patterns of people affected by CMT in India.
Through this initiative, we aim to strengthen CMT awareness and improve the representation of Indian patients in the global CMT community. Furthermore, the registry can support future research and help India prepare for clinical trials.
At the same time, strong awareness, collaboration, and patient participation can help build a stronger CMT community. Equally important, access to accurate and reliable information allows patients and families to make informed decisions. Together, these efforts can create new opportunities for CMT research and collaboration.
For transparency, all information shared on this page is intended for awareness and educational purposes only. In addition, we compile this information from publicly available and independently published sources.
Finally, if you have been diagnosed with CMT, please fill out the Patient Registration Form below.
Genetic Research
Studying unique Indian CMT variants to unlock targeted therapies.
Ongoing Research & Clinical Trials (by third-parties)
NMD670 (SYNAPSE-CMT)
Overview
NMD670 is an investigational small-molecule therapy being studied for its potential to improve neuromuscular function in individuals with neuromuscular disorders, including CMT.
Developed By
NMD Pharma
Research Focus
- Enhancing neuromuscular transmission
- Improving muscle strength and function
Current Status
Key Highlights
- Oral therapy
- Targets muscle function rather than genetic mutation
- Early-stage results show functional improvement potential
Source
Disclaimer
This study is conducted by independent organizations. We are only sharing publicly available information.
Drug Approval Process in India and World
