Global Research & Clinical Trials in Charcot-Marie-Tooth (CMT) Disease
Stay informed about ongoing research and future treatment possibilities.
At Charcot Marie Tooth Foundation of India, we aim to keep the patient community informed about ongoing research and clinical developments in Charcot-Marie-Tooth (CMT) disease across the world.
We are committed to improving awareness and access to reliable information related to CMT and ongoing global research efforts. This page provides a curated overview of international research initiatives, clinical trials, emerging therapies, scientific publications, and data-driven research approaches based on publicly available information from trusted sources.
Our platform highlights developments in areas such as gene therapy, drug development, neuromuscular rehabilitation, AI-based modeling, and patient-focused research initiatives to help patients, families, caregivers, healthcare professionals, and researchers stay updated on the latest progress in the field of CMT.
Disclaimer:
We do not conduct, fund, or manage the research projects or clinical trials mentioned on this website. All studies are carried out by independent researchers, institutions, and organizations. Information is shared solely for awareness and educational purposes.
In addition to sharing global research updates, we are also working toward building a National CMT Patient Data Registry in India to better understand the needs, experiences, and disease patterns of individuals affected by CMT within the Indian population. We believe such initiatives can help strengthen awareness, improve representation of Indian patients in the global CMT ecosystem, and support future research readiness.
We believe that awareness, collaboration, patient participation, and access to accurate information are important steps toward strengthening the CMT community and supporting future research opportunities. All information shared on this page is intended solely for awareness and educational purposes and is compiled from publicly available and independently published sources.
If you are diagnosed with CMT, please fill the following Patient Registration Form below:
Genetic Research
Studying unique Indian CMT variants to unlock targeted therapies.
Ongoing Research & Clinical Trials (by third-parties)
NMD670 (SYNAPSE-CMT)
Overview
NMD670 is an investigational small-molecule therapy being studied for its potential to improve neuromuscular function in individuals with neuromuscular disorders, including CMT.
Developed By
NMD Pharma
Research Focus
- Enhancing neuromuscular transmission
- Improving muscle strength and function
Current Status
Key Highlights
- Oral therapy
- Targets muscle function rather than genetic mutation
- Early-stage results show functional improvement potential
Source
Disclaimer
This study is conducted by independent organizations. We are only sharing publicly available information.
Drug Approval Process in India and World
